Translating Research Into Impact
Together we will find treatments and cures for children's genetic diseases
We partner with industry leaders to accelerate breakthrough therapies, transforming discoveries in genetics, gene therapy and cancer research into life-changing treatments for patients worldwide.
Advance your R&D pipeline through customised collaboration with our world-leading scientists. We design and execute innovative research projects that align with your therapeutic goals and accelerate development timelines.
Access our comprehensive portfolio of patented technologies, including cutting-edge gene therapy platforms, next-generation AAV capsids, advanced cell engineering solutions and early-stage potential cancer therapies to power your therapeutic programs.
Leverage our deep expertise in vector design, gene editing, vector production and sophisticated in vitro and in vivo models. Our state-of-the-art facilities and experienced teams are ready to accelerate your path to breakthrough treatments.
Connect with our Commercialisation Team to explore how our world-class research, resources and intellectual property can accelerate your therapeutic innovations.
By joining forces with leading research institutes, industry pioneers and healthcare organisations, we're accelerating the development of breakthrough genetic therapies and transforming how we treat childhood genetic diseases.
Collaboration to design and screen of capsid libraries to identify novel capsids for enhanced delivery of ocular gene therapies.
A spin-out company developing novel precision oncology medicines with the mission to turn cancer patients into cancer survivors.
Collaboration to develop novel bioengineered adeno-associated virus (AAV) capsids to route gene therapy directly to human cardiac muscle.
Collaboration to design and screen of capsid libraries to identify novel capsids for enhanced delivery of ocular gene therapies.
Patients into cancer survivors. Partnership with a clinical-stage biotechnology company to introduce gene therapy clinical trials for OTC-deficiency.
Collaboration to develop next-generation viral vectors for gene therapy and gene editing applications in liver and two other tissues.